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Findings on Healty Gene given to 12 adults w/CF

anonymous

New member
Has anyone heard about the findings of the Healthy Gene that was given to 12 adults w/CF (PHASE I). They were given a saline solution dripped slowly into the nasal passage. Investigators monitored salt transport in nose and determinded if the healthy gene was taken up by the cells and produced enough protein to affect the transport of salt and water in and out of cells. The findings of 2/3 of patients treated had an increase transport of chloride in nose. If all possible this could correct the defective CF cells. Also an aerosol version would enable CF pt's. to have the healthy gene delivered directly to lungs, which should provide superior treatment for the CF disease. Quotes from the CFF.org website, publications. Findings were to be presented at the American Society of Gene Therapy meeting in Washington, DC early June and CFF in Williamsburg end of May.Mother of 2 yr. old w/CF wishing for a better solution to CF. <img src="i/expressions/face-icon-small-smile.gif" border="0">
 

anonymous

New member
I read about it on the cff.org website under news, press release and look for a date of 4/29/03. It gives more detail in what is being done. I hope this is something that will work.Angie
 
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