G551D patients on Kalydeco

[musclemania70]

If you participated in the CCP for Kalydeco, when did you start it?
Thanks.

 

[musclemania70]

If you participated in the CCP for Kalydeco, when did you start it?
Thanks.

 

[LouLou]

What does CCP stand for?
Critical Control Point?
What phase is CCP?

I was in Ph. IIB and Ph. III and Open Label Extension

 

[LouLou]

What does CCP stand for?
Critical Control Point?
What phase is CCP?

I was in Ph. IIB and Ph. III and Open Label Extension

 

[musclemania70]

Compassionate Care Program.
I was wondering if there was anyone on here that started it prior to approval that was NOT in the study and the approximate date they started.

 

[musclemania70]

Compassionate Care Program.
I was wondering if there was anyone on here that started it prior to approval that was NOT in the study and the approximate date they started.

 

[musclemania70]

Oh, and if you participated in the study for kalydeco, did Vertex require you to be genotyped again prior to starting the study to verify they were indeed studying the accurate mutation? (more recently a person was incorrectly genotyped and found out they WERE g551d instead of homozygous f508)

 

[musclemania70]

Oh, and if you participated in the study for kalydeco, did Vertex require you to be genotyped again prior to starting the study to verify they were indeed studying the accurate mutation? (more recently a person was incorrectly genotyped and found out they WERE g551d instead of homozygous f508)