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Ataluren (PTC124) Are study participants close to finishing?

M

Mommafirst

Guest
I've been trying to keep up with the Atalauren stuff too, I've heard that the results were more promising in studies abroad than here (in the US) -- but that they weren't sure why there would be a difference. I hope it was just a study error in the US and that this is still a promising drug. My daughter also has a nonsense mutation.
 

missT

Member
I am just about hitting 5 weeks. The trial is supposed to go for 48 weeks and then open label. I know people who have started last feb. I believe that they are starting the open label sooner.
 

missT

Member
I am just about hitting 5 weeks. The trial is supposed to go for 48 weeks and then open label. I know people who have started last feb. I believe that they are starting the open label sooner.
 

missT

Member
I am just about hitting 5 weeks. The trial is supposed to go for 48 weeks and then open label. I know people who have started last feb. I believe that they are starting the open label sooner.
 
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