Gene therapy close in UK, but funds running out

[Mommafirst]

<div>I didn't realize that the gene therapy trials had seen much success...but now they are saying that if they can't raise the money the whole trial is going to fold.</div><div><br></div><a href="http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat">http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat</a>

 

[Mommafirst]

I didn't realize that the gene therapy trials had seen much success...but now they are saying that if they can't raise the money the whole trial is going to fold.<br><a href="http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat">http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat</a>

 

[Mommafirst]

I didn't realize that the gene therapy trials had seen much success...but now they are saying that if they can't raise the money the whole trial is going to fold.<br><a href="http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat">http://www.guardian.co.uk/science/2011/sep/18/cystic-fibrosis-cure-cash-threat</a>

 

[Havoc]

In the past, it hasn't. I participated in one study, the results weren't promising. This article seems poorly written to me, but I suppose it would to most of us, as it's written for the general public.

It seems to infer that the treatment is a new attempt at genetic therapy which has been in development in the UK for 10 years. As this would make the pharmaceutical company a buttload of money, I'm sure coming by any details will be difficult. I guess we'll have to wait and see.

 

[Havoc]

In the past, it hasn't. I participated in one study, the results weren't promising. This article seems poorly written to me, but I suppose it would to most of us, as it's written for the general public.

It seems to infer that the treatment is a new attempt at genetic therapy which has been in development in the UK for 10 years. As this would make the pharmaceutical company a buttload of money, I'm sure coming by any details will be difficult. I guess we'll have to wait and see.

 

[Havoc]

In the past, it hasn't. I participated in one study, the results weren't promising. This article seems poorly written to me, but I suppose it would to most of us, as it's written for the general public.
<br />
<br />It seems to infer that the treatment is a new attempt at genetic therapy which has been in development in the UK for 10 years. As this would make the pharmaceutical company a buttload of money, I'm sure coming by any details will be difficult. I guess we'll have to wait and see.

 

[alannae]

I know people are skeptical about gene therapy. We expected there to be more advancement by now (not just for CF) and more treatments available.<div><br></div><div>I am really surprised that there has not been more discussion on the forums here regarding the funding problem for the Gene Therapy Consortium in the UK. I mean, I don't care where the life-saving treatment comes from. I just want my daughter to live a long, happy, healthy life.</div><div><br></div><div>The theory behind the trials in the UK is different from that of the Vertex as is the method of administration. It is an inhaled/nebulized treatment not a pill.</div><div><br></div><div>What if this is the one that works? What if our children die because the money couldn't be raised? 6 million pounds to fund the next phase of development is not a lot of money to save the thousands of lives it could potentially save. What if we never find out whether it works or not?</div><div><br></div><div>This might be the opportunity that we have all been hoping for. It would be a real shame to never find out. It would be devastating to many of us.</div><div><br></div><div>Here is a link to the CF Trusts site for the emergency fundraising efforts <a href="http://www.cftrust.org.uk/gtappealnews/index.html#">http://www.cftrust.org.uk/gtappealnews/index.html#</a></div><div><br></div><div>My husband and I will be sending some of our donation money for this year to the UK to help their efforts. I sure hope that the CFF is watching this and will help keep the program going.</div>

 

[alannae]

I know people are skeptical about gene therapy. We expected there to be more advancement by now (not just for CF) and more treatments available.<br>I am really surprised that there has not been more discussion on the forums here regarding the funding problem for the Gene Therapy Consortium in the UK. I mean, I don't care where the life-saving treatment comes from. I just want my daughter to live a long, happy, healthy life.<br>The theory behind the trials in the UK is different from that of the Vertex as is the method of administration. It is an inhaled/nebulized treatment not a pill.<br>What if this is the one that works? What if our children die because the money couldn't be raised? 6 million pounds to fund the next phase of development is not a lot of money to save the thousands of lives it could potentially save. What if we never find out whether it works or not?<br>This might be the opportunity that we have all been hoping for. It would be a real shame to never find out. It would be devastating to many of us.<br>Here is a link to the CF Trusts site for the emergency fundraising efforts<a href="http://www.cftrust.org.uk/gtappealnews/index.html#">http://www.cftrust.org.uk/gtappealnews/index.html#</a><br>My husband and I will be sending some of our donation money for this year to the UK to help their efforts. I sure hope that the CFF is watching this and will help keep the program going.

 

[alannae]

I know people are skeptical about gene therapy. We expected there to be more advancement by now (not just for CF) and more treatments available.<br>I am really surprised that there has not been more discussion on the forums here regarding the funding problem for the Gene Therapy Consortium in the UK. I mean, I don't care where the life-saving treatment comes from. I just want my daughter to live a long, happy, healthy life.<br>The theory behind the trials in the UK is different from that of the Vertex as is the method of administration. It is an inhaled/nebulized treatment not a pill.<br>What if this is the one that works? What if our children die because the money couldn't be raised? 6 million pounds to fund the next phase of development is not a lot of money to save the thousands of lives it could potentially save. What if we never find out whether it works or not?<br>This might be the opportunity that we have all been hoping for. It would be a real shame to never find out. It would be devastating to many of us.<br>Here is a link to the CF Trusts site for the emergency fundraising efforts<a href="http://www.cftrust.org.uk/gtappealnews/index.html#">http://www.cftrust.org.uk/gtappealnews/index.html#</a><br>My husband and I will be sending some of our donation money for this year to the UK to help their efforts. I sure hope that the CFF is watching this and will help keep the program going.