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Gene Therapy

jdubbs

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Just in case you hadn't heard, I think G551D is what VX770 is effective on. I'm not sure if you need two copies or just one.
 

jdubbs

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">http://www.cff.org/aboutCFFoun...cfm?ID=9916&TYPE=1670
</a>

Just in case you hadn't heard, I think G551D is what VX770 is effective on. I'm not sure if you need two copies or just one.
 

jdubbs

New member
<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/aboutCFFoundation/NewsEvents/index.cfm?ID=9916&TYPE=1670
">http://www.cff.org/aboutCFFoun...cfm?ID=9916&TYPE=1670
</a>

Just in case you hadn't heard, I think G551D is what VX770 is effective on. I'm not sure if you need two copies or just one.
 

jdubbs

New member
<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/aboutCFFoundation/NewsEvents/index.cfm?ID=9916&TYPE=1670
">http://www.cff.org/aboutCFFoun...cfm?ID=9916&TYPE=1670
</a>

Just in case you hadn't heard, I think G551D is what VX770 is effective on. I'm not sure if you need two copies or just one.
 

jdubbs

New member
<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/aboutCFFoundation/NewsEvents/index.cfm?ID=9916&TYPE=1670
">http://www.cff.org/aboutCFFoun...cfm?ID=9916&TYPE=1670
</a><br />
<br />
<br />Just in case you hadn't heard, I think G551D is what VX770 is effective on. I'm not sure if you need two copies or just one.
 

LouLou

New member
That's it JD thanks! I'll read it now.

Yes, Katie it is tragic that sometimes clinical trials result in unpleasant outcomes. The thing is usually - and in the case of the gene therapy in the past - the deaths were in early trials which don't involve many people and often they recruit people that are in late stage cf I do believe. And of course studies are always conducted on animals first and most side effects are discovered before going into people.

I heard recently that 1/3 of the cf population is going to have to participate in clinical trials in order to keep up with the pace that meds/treatments are moving through the pipeline. We all need to deeply consider trial participation. I was in the Vertex VX-770 2b trial and it was a great experience.

Always remember that you'll receive a detailed description about the med & known side effects before participation consent and you can always bail out at any point.

In my opinion, more of us should move ahead with paricipation, gather info and then make a decision. To sit back and think that all are the same and either you should or shouldn't participate is naive. Each one has intricacies that could make it really great or not so for you to participate.
 

LouLou

New member
That's it JD thanks! I'll read it now.

Yes, Katie it is tragic that sometimes clinical trials result in unpleasant outcomes. The thing is usually - and in the case of the gene therapy in the past - the deaths were in early trials which don't involve many people and often they recruit people that are in late stage cf I do believe. And of course studies are always conducted on animals first and most side effects are discovered before going into people.

I heard recently that 1/3 of the cf population is going to have to participate in clinical trials in order to keep up with the pace that meds/treatments are moving through the pipeline. We all need to deeply consider trial participation. I was in the Vertex VX-770 2b trial and it was a great experience.

Always remember that you'll receive a detailed description about the med & known side effects before participation consent and you can always bail out at any point.

In my opinion, more of us should move ahead with paricipation, gather info and then make a decision. To sit back and think that all are the same and either you should or shouldn't participate is naive. Each one has intricacies that could make it really great or not so for you to participate.
 

LouLou

New member
That's it JD thanks! I'll read it now.

Yes, Katie it is tragic that sometimes clinical trials result in unpleasant outcomes. The thing is usually - and in the case of the gene therapy in the past - the deaths were in early trials which don't involve many people and often they recruit people that are in late stage cf I do believe. And of course studies are always conducted on animals first and most side effects are discovered before going into people.

I heard recently that 1/3 of the cf population is going to have to participate in clinical trials in order to keep up with the pace that meds/treatments are moving through the pipeline. We all need to deeply consider trial participation. I was in the Vertex VX-770 2b trial and it was a great experience.

Always remember that you'll receive a detailed description about the med & known side effects before participation consent and you can always bail out at any point.

In my opinion, more of us should move ahead with paricipation, gather info and then make a decision. To sit back and think that all are the same and either you should or shouldn't participate is naive. Each one has intricacies that could make it really great or not so for you to participate.
 

LouLou

New member
That's it JD thanks! I'll read it now.

Yes, Katie it is tragic that sometimes clinical trials result in unpleasant outcomes. The thing is usually - and in the case of the gene therapy in the past - the deaths were in early trials which don't involve many people and often they recruit people that are in late stage cf I do believe. And of course studies are always conducted on animals first and most side effects are discovered before going into people.

I heard recently that 1/3 of the cf population is going to have to participate in clinical trials in order to keep up with the pace that meds/treatments are moving through the pipeline. We all need to deeply consider trial participation. I was in the Vertex VX-770 2b trial and it was a great experience.

Always remember that you'll receive a detailed description about the med & known side effects before participation consent and you can always bail out at any point.

In my opinion, more of us should move ahead with paricipation, gather info and then make a decision. To sit back and think that all are the same and either you should or shouldn't participate is naive. Each one has intricacies that could make it really great or not so for you to participate.
 

LouLou

New member
That's it JD thanks! I'll read it now.
<br />
<br />Yes, Katie it is tragic that sometimes clinical trials result in unpleasant outcomes. The thing is usually - and in the case of the gene therapy in the past - the deaths were in early trials which don't involve many people and often they recruit people that are in late stage cf I do believe. And of course studies are always conducted on animals first and most side effects are discovered before going into people.
<br />
<br />I heard recently that 1/3 of the cf population is going to have to participate in clinical trials in order to keep up with the pace that meds/treatments are moving through the pipeline. We all need to deeply consider trial participation. I was in the Vertex VX-770 2b trial and it was a great experience.
<br />
<br />Always remember that you'll receive a detailed description about the med & known side effects before participation consent and you can always bail out at any point.
<br />
<br />In my opinion, more of us should move ahead with paricipation, gather info and then make a decision. To sit back and think that all are the same and either you should or shouldn't participate is naive. Each one has intricacies that could make it really great or not so for you to participate.
 

laulau555

New member
thanks JD what a hopeful thing to read in the morning! ...hmm maybe i'll have to move to the uk if this doesn't start happening in the us!
 

laulau555

New member
thanks JD what a hopeful thing to read in the morning! ...hmm maybe i'll have to move to the uk if this doesn't start happening in the us!
 

laulau555

New member
thanks JD what a hopeful thing to read in the morning! ...hmm maybe i'll have to move to the uk if this doesn't start happening in the us!
 

laulau555

New member
thanks JD what a hopeful thing to read in the morning! ...hmm maybe i'll have to move to the uk if this doesn't start happening in the us!
 

laulau555

New member
thanks JD what a hopeful thing to read in the morning! ...hmm maybe i'll have to move to the uk if this doesn't start happening in the us!
 
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